International Rett Syndrome Foundation

January 9, 2024

VUMC receives $13 million grant to coordinate multisite clinical trial for Rett syndrome treatment

Vanderbilt University Medical Center received a $13 million Department of Defense grant to lead a multisite clinical trial that will evaluate repurposed FDA-approved drugs as treatment options for patients with Rett syndrome.

March 3, 2016

Study reveals possible ‘dimmer switch’ drug for Rett syndrome

Researchers at Vanderbilt University Medical Center have relieved symptoms in a mouse model of Rett syndrome with a drug-like compound that works like the dimmer switch in an electrical circuit.