sickle cell disease

(iStock image)

Blood formation and disorders expert Stuart Orkin to present Discovery Lecture March 27

Orkin’s research led to a gene therapy for sickle cell disease and beta-thalassemia; it is the first Food and Drug Administration-approved CRISPR-based gene therapy.

(iStock)

VUMC part of new study validating curative therapy for sickle cell disease

Of 38 adults with severe SCD who participated in the study, more than 97% no longer required immunosuppressive therapy one year after the transplant.

International trial introduces another curative option for sickle cell disease 

The therapy, haploidentical bone marrow transplant with thiotepa and posttransplant cyclophosphamide, is as safe and more affordable than the recently FDA-approved myeloablative gene therapy and gene editing treatments.

(iStock image)

VUMC hosts symposium on stem cell transplants and cellular therapies

The Vanderbilt Stem Cell Transplant and Cellular Therapy Symposium offers clinicians detailed information on the latest developments for hematological diseases, ranging from immunotherapies for blood cancers to new, curative therapies for sickle cell disease.

Michael DeBaun, MD, MS, MPH

VUMC’s DeBaun elected president-elect of the American Pediatric Society

Vanderbilt’s Michael DeBaun, MD, MS, MPH, has been elected president-elect of the American Pediatric Society.

No detail is too small and no task too big for research administrative officer Mustafa Nateqi

Nateqi’s can-do attitude and dedication earn him a Credo Award.

1 2