The first drug to treat the symptoms of Rett syndrome was recently approved, following a Nature Medicine study publishing results from the pivotal phase 3 LAVENDER study led by investigators from Vanderbilt University Medical Center to evaluate efficacy and safety of trofinetide.

After nearly 40 years and being involved in more than 300 lifesaving transplantations at Monroe Carell Jr. Children’s Hospital at Vanderbilt, Debra Dodd, MD, is retiring.

Using a four-dimensional microscope that allows them to watch a tissue putting itself together, researchers at Vanderbilt University Medical Center have achieved a rare feat in science — they have shattered a long-standing dogma about how the lung develops.

Monroe Carell Jr. Children’s Hospital at Vanderbilt recently hosted the first statewide conference of the Tennessee Pediatric Neurocritical Care Collaboration.

The Vanderbilt Kennedy Center (VKC) has announced new leadership for its University Center for Excellence in Developmental Disabilities (UCEDD). Julie Lounds Taylor, PhD, and Pablo Juárez, MEd, BCBA, LBA, have succeeded Elise McMillan, JD, who retired June 30.

New research shows that about half of pediatric patients who died of sepsis over the past 20 years at Vanderbilt University Medical Center had evidence of an inflammatory state called persistent inflammation, immunosuppression and catabolism syndrome.

Genetic mosaicism — when the body’s cells do not all have the same genetic makeup — could generate variants previously thought to be spontaneous in genetic disease, and detecting parental mosaicism could clarify recurrence risk for future children.